The Minister of Health, Alexandru Rogobete, emphasizes that, in the case of rare diseases, each new therapeutic option can change the course of some lives, which is why access to modern treatments is essential.

Alexandru Rogobete emphasizes the difficulties faced by patients with rare diseases, who often encounter a lack of clear information and long journeys between specialists. Access to modern treatments is crucial, as they can transform the lives of affected families. Among the new therapies available is Vosoritidum, the first reimbursed treatment in Romania for achondroplasia. Efgartigimodum alfa offers a solution for patients with myasthenia gravis, stabilizing the progression of the disease. Berotralstatum provides an option for preventing attacks of hereditary angioedema, while Vutrisiranum slows the progression of hereditary amyloidosis. Additionally, Filgotinibum becomes a modern option for patients with ulcerative colitis. These advances demonstrate the commitment to providing better solutions and improving the quality of life for patients.